Gene Therapy With URO-902 (pVAX/

Document Type

Article

Publication Date

12-18-2024

Publication Title

The Journal of urology

Abstract

PURPOSE: To assess efficacy and safety of URO-902, an investigational gene therapy expressing the α subunit of the large-conductance Ca

MATERIALS AND METHODS: Women, 40‒79 years, with OAB and urge urinary incontinence (UUI) who were refractory to OAB medications were randomized to single-dose URO-902 24 and 48 mg or placebo administered by intradetrusor injection via cystoscopy under local anesthesia. Efficacy endpoints included change from baseline to week 12 in mean daily micturitions, urgency episodes, UUI episodes, and patient-reported outcomes. Safety assessments included adverse events (AEs) and postvoid residual urine volume.

RESULTS: Of 80 patients randomized (URO-902 24 mg, n=26; URO-902 48 mg, n=27; placebo, n=27), 74 received treatment, and 67 reached week 24. At week 12, URO-902 24 and 48 mg were associated with significant improvement vs placebo in daily micturitions (least squares mean change from baseline, -2.3 and -2.4 vs -0.8; least square mean difference [95% confidence interval], ‒1.5 [‒2.7 to ‒0.3] and ‒1.6 [‒2.8 to ‒0.4], nominal

CONCLUSIONS: In this phase 2a trial, treatment with URO-902 was associated with improvements vs placebo in efficacy and patient-reported outcomes and was safe and well tolerated.

First Page

101097

DOI

10.1097/JU.0000000000004373

ISSN

1527-3792

PubMed ID

39693268

Share

COinS